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Dr. Smith

Dr. Smith

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Eureka!

FDA approves milestone treatments for sickle cell disease

Two breakthrough gene therapies can now be used to treat and possibly cure sickle cell anemia, the genetic blood disorder that afflicts 100,000 mostly Black Americans and 20 million people worldwide. But the announcement from the Food and Drug Administration of approval of the treatments — the first use of medicines to address an inherited disease — drew cheers and caution flags from those in the field.